Donations

NTSAD Stay-At-Home-Gala

NTSAD Research Needs Your Help Now!

Tay-Sachs disease is always fatal in children and progressively disabling in adult onset forms. Tay-Sachs disease research is at a critical point to move forward to treatment and cure never before thought possible. With your help, the Tay-Sachs Gene Therapy Consortium (TSGT) clinical human trials could begin as early as September 2012.

Exceptional, promising therapeutic results have been obtained in several animal models.
Cats with GM2 gangliosidosis, who usually die by 3.5 to 4.5 months of age and cannot move, see, or use a litter box, are still alive and reasonably healthy at ages 12.0 to 18.8 months.
Sheep with Tay-Sachs generally die at age 7-8 months; treated sheep lived almost twice as long.
Based on this demonstrated proof of concept in animal models, the TSGT believes that it can achieve the other milestones required to begin human clinical trials.
Positive feedback was received from officials at the FDA.

The need is urgent as new children continue to be born with Tay-Sachs disease. This research project brings real hope for a treatment and cure and the potential for this gene therapy model to work for other neuro-degenerative diseases such as Multiple Sclerosis, Parkinson's and Alzheimer's disease.

The only obstacle at this time is the unfunded portion of the project - $350,000 is still needed to complete all necessary studies with the goal to reach the clinical human trial by September 2012. Visit our website www.ntsad-ny.org for further information.

Please join the fight! Your support will bring us closer to treatment and cure and will really make a difference in the lives of those families affected by Tay-Sachs and other related genetic diseases. Please help now!

You can partcipate by filling out the form below, or printing out a copy and mailing your payment in.